A functionally active retrovirus vector for gene therapy in Fanconi anemia group C

Biochemical transfer of single-copy eucaryotic genes using total cellular DNA as donor

1978 • 1,284 citations

Redesign of Retrovirus Packaging Cell Lines To Avoid Recombination Leading to Helper Virus Production

1986 • 1,276 citations

A safe packaging line for gene transfer: separating viral genes on two different plasmids

1988 • 1,118 citations

Helper virus induced T cell lymphoma in nonhuman primates after retroviral mediated gene transfer.

1992 • 544 citations

Rapid Cell Culture Assay Technique for Murine Leukaemia Viruses

1971 • 360 citations

Evidence for at least four Fanconi anaemia genes including FACC on chromosome 9

1992 • 305 citations

Leukemia and preleukemia in Fanconi anemia patients

1991 • 268 citations

Long-term in vivo expression of a murine adenosine deaminase gene in rhesus monkey hematopoietic cells of multiple lineages after retroviral mediated gene transfer into CD34+ bone marrow cells

1993 • 185 citations

A common mutation in the FACC gene causes Fanconi anaemia in Ashkenazi Jews

1993 • 171 citations

Retroviral-mediated gene transfer into CD34-enriched human peripheral blood stem cells.

1993 • 154 citations

Mutation analysis of the Fanconi anemia gene FACC.

1994 • 130 citations

FANCONI'S ANAEMIA AND ITS VARIABILITY

1993 • 121 citations

A nonsense mutation and exon skipping in the Fanconi anaemia group C gene

1993 • 91 citations

The use of NaOH as transfer solution of DNA onto nylon membrane decreases the hybridization efficiency

1987 • 89 citations

Factors Affecting Retroviral Vector Function and Structural Integrity

1993 • 87 citations

Cloning and analysis of the murine Fanconi anemia group C cDNA

1993 • 75 citations

Bone marrow transplantation for Fanconi anemia using low-dose cyclophosphamide/thoracoabdominal irradiation as conditioning regimen: chimerism study by the polymerase chain reaction

1993 • 55 citations

Etiologic Mechanisms of Hematopoietic Failure

1990 • 18 citations

A trial of recombinant human superoxide dismutase in patients with Fanconi anaemia

1993 • 13 citations

Mapping of the murine and rat Facc genes and assessment of flexed-tail as a candidate mouse homolog of Fanconi anemia group C

1993 • 11 citations