Long-term Clinical Outcome of Patients with Severe Combined Immunodeficiency Who Received Related Donor Bone Marrow Transplants without Pretransplant Chemotherapy or Post-transplant GVHD Prophylaxis

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1999 • 713 citations

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2003 • 575 citations

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1993 • 338 citations

Hematopoietic stem cell transplantation for severe combined immunodeficiency in the neonatal period leads to superior thymic output and improved survival

2002 • 330 citations

Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency

2009 • 237 citations

Development of immunity in human severe primary T cell deficiency following haploidentical bone marrow stem cell transplantation.

1986 • 199 citations

Long-Term Chimerism and B-Cell Function After Bone Marrow Transplantation in Patients With Severe Combined Immunodeficiency With B Cells: A Single-Center Study of 22 Patients

1999 • 123 citations

Influence of severe combined immunodeficiency phenotype on the outcome of HLA non-identical, T-cell–depleted bone marrow transplantationA retrospective European survey from the European Group for Bone Marrow Transplantation and the European Society for Immunodeficiency

1999 • 120 citations

Long-term immune reconstitution and clinical outcome after stem cell transplantation for severe T-cell immunodeficiency

2007 • 101 citations

Cognitive and behavioral abnormalities in children after hematopoietic stem cell transplantation for severe congenital immunodeficiencies

2008 • 99 citations

Gene therapy improves immune function in preadolescents with X-linked severe combined immunodeficiency

2007 • 99 citations

Patients with adenosine deaminase deficiency surviving after hematopoietic stem cell transplantation are at high risk of CNS complications

2006 • 99 citations

Early determinants of long-term T-cell reconstitution after hematopoietic stem cell transplantation for severe combined immunodeficiency

2006 • 77 citations

Thymic output, T-cell diversity, and T-cell function in long-term human SCID chimeras

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Thyroid dysfunction after bone marrow transplantation for primary immunodeficiency without the use of total body irradiation in conditioning

2004 • 67 citations

Long-term immune reconstitution after anti-CD52–treated or anti-CD34–treated hematopoietic stem cell transplantation for severe T-lymphocyte immunodeficiency

2007 • 53 citations

Long-term outcomes of nonconditioned patients with severe combined immunodeficiency transplanted with HLA-identical or haploidentical bone marrow depleted of T cells with anti-CD6 mAb

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2001 • 26 citations