Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for hemophilia B.

The Metabolic Basis of Inherited Disease.

1988 • 7,933 citations

Construction of a retrovirus packaging mutant and its use to produce helper-free defective retrovirus

1983 • 1,857 citations

The Metabolic Basis of Inherited Diseases

1972 • 1,762 citations

Redesign of Retrovirus Packaging Cell Lines To Avoid Recombination Leading to Helper Virus Production

1986 • 1,276 citations

Safe and efficient generation of recombinant retroviruses with amphotropic and ecotropic host ranges.

1988 • 908 citations

Site-Specific Gene Expression in Vivo by Direct Gene Transfer into the Arterial Wall

1990 • 573 citations

Self-inactivating retroviral vectors designed for transfer of whole genes into mammalian cells.

1986 • 533 citations

Progress Toward Human Gene Therapy

1989 • 484 citations

An alternative approach to somatic cell gene therapy.

1988 • 198 citations

Production of human factor IX in animals by genetically modified skin fibroblasts: potential therapy for hemophilia B

1989 • 177 citations

Correction of the genetic defect in hepatocytes from the Watanabe heritable hyperlipidemic rabbit.

1988 • 155 citations

Progress toward human gene therapy

1990 • 127 citations

Expression of human factor IX in rabbit hepatocytes by retrovirus-mediated gene transfer: potential for gene therapy of hemophilia B.

1990 • 94 citations

Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs.

1990 • 90 citations

Regulation of insulin receptor internalization in vascular endothelial cells by insulin and phorbol ester.

1987 • 83 citations

Expression of active human factor IX in transfected cells

1985 • 82 citations

Human genes for complement components C1r and C1s in a close tail-to-tail arrangement.

1988 • 79 citations

Enhancement of the fibrinolytic activity of sheep endothelial cells by retroviral vector-mediated gene transfer

1991 • 62 citations

Correction of CD18-Deficient Lymphocytes by Retrovirus-Mediated Gene Transfer

1990 • 60 citations

Structural and functional basis of the developmental regulation of human coagulation factor IX gene: factor IX Leyden.

1990 • 44 citations

Characterization of a Mouse Factor IX cDNA and Developmental Regulation of the Factor IX Gene Expression in Liver

1991 • 31 citations

Towards gene therapy for hemophilia B.

1987 • 29 citations

Blood vessel wall and thrombosis

1988 • 19 citations

Recombinant Antihemophilic Factors

1991 • 10 citations